Websites using rare disease as a keyword

Perlara PBC is a scientific discovery company finding treatments for rare diseases previously believed to be too rare to cure.

Pharmaceutical market access, Business Development, distribution &Pharmaceutical consultancy in the Middle East & North Africa region for specialty

Rare disease information gateway, support groups directory, practical advice, health and disability resources, research information, news and issues.

The Wilson Disease Association (WDA) is a volunteer organization striving to promote the well being of patients with Wilson disease and their families and friends.

Support, resources and encouragement for people with rare diseases

Spherix Global Insights - independent business intelligence and market research company specializing in renal, autoimmune, neurologic, rare disease markets.

Behcets Syndrome Society - caring for those with a rare and complex disease

Fastest Growing Company in Pittsburgh & Top 10 Nationwide - PANTHERx Specialty Pharmacy is the Rare Disease Specialty Pharmacy based in Pittsburgh, PA

Meet a community of people living with cystinosis. Learn what causes this rare, genetic disease, ways to manage, treatment options, and the latest tips & advice

Rare Disease United's mission is to build a strong rare disease community throughout the USA, help provide support, information raise awareness & advocate for families.

The first + only thought leader engagement + education company exclusively dedicated to Oncology + RareDisease

RareConnect promotes global conversation and collaboration to improve the lives of rare disease patients and assist the organizations that serve them. RareConnect is an online social network for patients and families who live with one of over 6,000 rare diseases to connect with one and other to support and share vital experiences on aspects of living with a rare disease. Organized into disease specific communities, the platform also provides links to quality information, clinical trials and research publications and provides an opportunity for international networking and collaboration between patient organizations.

Rare Disease UK (RDUK) is the national campaign for people with rare diseases and all who support them. We believe that everyone living with a rare disease should be able to receive high quality services, treatment and support.

"A Cure for Ellie" is a registered non-profit organization dedicated to raising awareness and funds for research into LBSL,

The Lysosomal Disease Network is an NIH-funded research network working to create effective treatments and/or cures for the lysosomal diseases, which are 70+ hereditary metabolic diseases. The Lysosomal Disease Network is headquartered at the University of Minnesota, with participating research institutions located from coast to coast in the United States of America.

The Addison’s Disease Self-Help Group (ADSHG) is the support group for people with Addison's disease and their families in the UK and Ireland. It aims to support its members and those with Addison's disease, to promote better medical understanding of this rare condition, working in co-operation with leading adrenal specialists. Registered as a UK charity and founded 1984.<br />

JP2MRI is a non-profit medical research institute devoted to find cures for medical diseases for the use of ethical adult stem cells.

The Alliance For Cryoglobulinemia works to connect Patients. We want to help you understand how to live with Cryoglobulinemia. Cryoglobulinemia is a rare disease.

Dying, surviving, and aging with grace. Not necessarily in that order Resources on illness, death and dying, loss, grief, and positive aging

Aparito uses wearable technology and disease specific mobile apps to monitor patients outside of the hospital

Join the National Organization for Rare Disorders (NORD) in raising awareness for the 30 million patients with rare diseases in the U.S. on Rare Disease Day®.

A blog about the grief after losing a child to Niemann Pick, Type C, a rare disease, and how I'm moving forward with my life

Lifestyle of a simple father of 3

Rare Disease Specialty and Home Infusion Pharmacy

Myasthenia Gravis Foundation of Michigan is committed to finding a cure for Myasthenia Gravis and closely related disorders, improving treatment options and providing information and support to people with Myasthenia Gravis through research, education, community programs, and advocacy.

EURORDIS - Rare Diseases Europe, is a non-governmental patient-driven alliance of rare disease patient organisations representing 745 rare diseases patient organisations in 65 countries. We are dedicated to improving the quality of life of all people living with rare diseases in Europe

Generalised and partial lipodystrophy (GL and PL)

The Pulmonary Hypertension Association is the leading organization connecting PH patients, families, and medical professionals. PHA provides hope to the PH community by improving patient lives and working towards a cure.

Enter a patient's clinical signs and symptoms to narrow down a rare disease diagnosis.

Raising awareness about Corticalbasal Degeneration (CBD), a rare neurological disease

a rare disease, a wonderful life

Special Needs Jungle provides parent-centred information, news, special needs resources and informed opinion about SEND - Special education needs and disability, Education, Health and Care Plans, children's physical and mental health including rare disease and SEN politics

Global Genes is a leading rare disease advocacy organization with global reach to the worldwide rare community of patients, caregivers, advocates and clinical partners. Our mission is to eliminate the challenges of rare disease.

Rare Diseases South Africa a registered NPO organization which assists rare disease patients receive access to life-saving treatment and supportive care.

Find an expert doctor or hospital for any rare disease. We analyzed 55 billion data points before providing you with a personalized 360 degree evaluation of a doctor.

In rare disease, you are not alone. We connect families with up-to-date scientific information, community insights and clinical trials.

ilPolmone.it fornisce informazioni su malattie rare polmonari come istiocitosi, fibrosi, ipertensione e linfangioleiomiomatosi. Articoli, materiale divulgativo e presentazioni di convegni su diagnosi e cura di pneumopatologie.E non solo: interviene anche su temi come smog e salute, danni da fumo, asma e allergie.Curato dallo staff del dottor Harari, primario di pneumologia presso l'Ospedale San Giuseppe di Milano.

Alstrom Angels

We offer complete therapy management support to help Pharma brands develop better patient experiences and outcomes. We design multi-channel patient experiences using phone, web, mobile and printed materials to engage patients and family on your behalf.

WeHealth empowers you to become advocates using social media and rewards you for helping patients. Join WeHealth's network of advocates to connect rare disease patients with answers, support, & treatments!

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Ultra rare disease foundation is here to help you find more information about Ultra rare diseases as well as help you connect with families experiencing a similar life

The Dylan Flinchum Rock On! Foundation supports a boy suffering from metachromatic leukodystrophy (MLD) and his family, and hosts events like the Dinosaur Stomp 5k to raise awareness about this rare disease.

Chocolate Bar means awesome to the 6 year old author whose goal is to raise money to cure his friend’s rare disease.

Explore Daelmann, Rare disease and specialty pharmaceutical comparators for global, adaptive, and patient-centered clinical trials, Delivered!

By combining knowledge of the marketplace, science, instructional design, and delivery technologies, we deliver training that results in greater competence and confidence in Sales, Medical Affairs, and R&D professionals.

FutureNeuro is an SFI Research Centre to develop new technologies and solutions for the treatment, diagnosis, and monitoring of chronic and rare neurological diseases.

International Journal of Case Reports and Images (IJCRI) is an international, peer reviewed, monthly, open access, online journal, publishing high-quality, peer reviewed articles in all areas of basic medical sciences and clinical specialties.Aim of IJCRI is to encourage the publication of new information by providing a platform for reporting of unique, unusual and rare cases which enhance understanding of disease process, its diagnosis, management and clinico-pathologic correlations.Following types of articles are published in IJCRI: Review Articles, Case Series, Case Reports, Case in Images, Clinical Images and Letter to Editors.

Dr. John G. McHenry is committed to the treatment, prevention and rehabilitation of neurologically related eye diseases and vision disorders. He is a leading Interventional Neuro-ophthalmologist who has trained the next generation of eye doctors in Oculoplastics, Orbital Surgery and the medical and surgical care of double vision. Dr. McHenry is the only interventional neuro-ophthalmologist in North Texas. He sees patient from all over North, East and West Texas as well as the Hill country, the Valley, the Panhandle, New Mexico, Oklahoma, Arkansas, Kansas, Missouri, Louisiana and Mississippi and consults on rare and complicated eye conditions across the country.

IR Innovate Research is a privately owned Indian Clinical Research Organisation (CRO) based in Noida.

CSL Limited is a global, specialty biopharmaceutical company that researches, develops, manufactures and markets products to treat and prevent serious human medical conditions

Visit the virtualmedstudent.com for information on all aspects of health. Tutorials on both common and rare condition in easy to understand language. In addition, visit our video page for videos about common health issues.

MHE Research Foundation 501(c)(3) organization dedicated to finding a cure for this rare bone disease. Providing comprehensive information on Research, Orthopaedics, Genetics, Chronic Pain, Conferences and Doctor Directories to help locate medical care.

Life's a Polyp is a personal health blog of my journey with Familial Adenomatous Polyposis, a rare genetic disease resulting in cancer & other issues.

When someone is diagnosed with mesothelioma, This is a disease that is rare, and there is little to be said about the condition.

The Smith Family Clinic for Genomic Medicine has been established to use whole genome sequencing to diagnose rare, undiagnosed and misdiagnosed disease.

CSL Limited is a global, specialty biopharmaceutical company that researches, develops, manufactures and markets products to treat and prevent serious human medical conditions

AFM-Téléthon is an association composed of patients and their families who are affected by a genetic, rare, progressive and severely disabling disease

Enzyvant is a biopharmaceutical company focused on the development of transformative therapies for rare diseases with high unmet needs.

To empower rare & undiagnosed patients and their families with genomic information and community through advocacy, networking and support.

Cure Sanfilippo, Gene therapy, Get help for Sanfilippo, MPS, MPS III, Rare diseases, lysosomal disease, and Fundraising

Leading provider of global genomic research services and market leader for genetic diagnostic testing. Our unique access to genomics data with clinical and phenotypic information provides insights into complex diseases at the genetic and molecular level to facilitate research in personalized healthcare. We have dedicated genomic solutions in cancer immunotherapy, diabetes and rapidly expanding into other disease areas including ophthalmology, neurology and rare diseases.

StudyPages is a self-service study listing platform to quickly set up a dedicated webpage for a research study, share with target communities using social media, and track signups. StudyPages by Yuzu Labs was created to bring human research online, accelerate it, and make it part of everyone's daily life.

Neuroendocrine cancer and carcinoid disease information for patients Health care providers and rare cancer

Fabry disease is a rare genetic disorder and a life-threatening condition. Learn about the signs, symptoms, inheritance, genetics, and treatment.

Keeping the spirit alive amidst life's difficult trials