Websites using rare diseases as a keyword

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Soligenix, Inc. is a late-stage biopharmaceutical company focused on developing and commercializing products to treat rare diseases where there is an unmet medical need.

Join the National Organization for Rare Disorders (NORD) in raising awareness for the 30 million patients with rare diseases in the U.S. on Rare Disease Day®.

We are a Swiss specialty pharmaceutical company committed to developing medicines to meet the needs of patients living with mitochondrial disorders and other rare diseases.

Lysosomal Diseases New Zealand

Ultragenyx is a clinical-stage biopharmaceutical company committed to bringing to market novel products for the treatment of rare and ultra-rare diseases, with a focus on serious, debilitating genetic diseases. Founded in 2010, the company has rapidly built a diverse portfolio of product candidates with the potential to address diseases for which the unmet medical need is high, the biology for treatment is clear, and for which there are no approved therapies.

Bringing hope and relief to patients with undertreated rare diseases through the development and commercialization of curative first-in-class gene-modified cell therapies.

To empower rare & undiagnosed patients and their families with genomic information and community through advocacy, networking and support.

Find an expert doctor or hospital for any rare disease. We analyzed 55 billion data points before providing you with a personalized 360 degree evaluation of a doctor.

Cure Sanfilippo, Gene therapy, Get help for Sanfilippo, MPS, MPS III, Rare diseases, lysosomal disease, and Fundraising

At ARG, we connect individuals with rare diseases to organizations driven to develop potential treatments. We advance smarter clinical trials.

RareConnect promotes global conversation and collaboration to improve the lives of rare disease patients and assist the organizations that serve them. RareConnect is an online social network for patients and families who live with one of over 6,000 rare diseases to connect with one and other to support and share vital experiences on aspects of living with a rare disease. Organized into disease specific communities, the platform also provides links to quality information, clinical trials and research publications and provides an opportunity for international networking and collaboration between patient organizations.

Centro de Investigación Biomédica en Red de Enfermedades Raras CIBERER

Our purpose is to enable people with life-altering conditions to lead better lives. Explore our pioneering therapies, vision, and values at shire.com.

Enzyvant is a biopharmaceutical company focused on the development of transformative therapies for rare diseases with high unmet needs.

The Lysosomal Disease Network is an NIH-funded research network working to create effective treatments and/or cures for the lysosomal diseases, which are 70+ hereditary metabolic diseases. The Lysosomal Disease Network is headquartered at the University of Minnesota, with participating research institutions located from coast to coast in the United States of America.

Our purpose is to enable people with life-altering conditions to lead better lives. Explore our pioneering therapies, vision, and values at shire.com.

Caylum willemse was born with TOF and OA and tracheobronchomalacia and needs another operation to live which only can be done by a Doctor from Boston

Alexion is focused on developing and delivering life-transforming therapies for patients with devastating and rare diseases.

Alexion is focused on developing and delivering life-transforming therapies for patients with devastating and rare diseases.

Parent Project Muscular Dystrophy's mission is to end Duchenne muscular dystrophy. We accelerate research, raise our voices in Washington, demand optimal care for all young men, and educate the global community.

PowerPoint Presentations university of health sciences ppt medical images and illustrations OSPE OSCE free medical ebooks medical books MBBS

Rare Disease UK (RDUK) is the national campaign for people with rare diseases and all who support them. We believe that everyone living with a rare disease should be able to receive high quality services, treatment and support.

NORD, a 501(c)(3) organization, is the leading patient advocacy organization dedicated to improving the lives of individuals and families living with rare diseases.

Support, resources and encouragement for people with rare diseases

Rare Diseases South Africa a registered NPO organization which assists rare disease patients receive access to life-saving treatment and supportive care.

Leading provider of global genomic research services and market leader for genetic diagnostic testing. Our unique access to genomics data with clinical and phenotypic information provides insights into complex diseases at the genetic and molecular level to facilitate research in personalized healthcare. We have dedicated genomic solutions in cancer immunotherapy, diabetes and rapidly expanding into other disease areas including ophthalmology, neurology and rare diseases.

РООИ "Здоровье Человека"

Skin-diseases.org helps you to get complete cure for various skin diseases and disorders types, problems and common conditions including treatment methods and prevention tips.

CSL Limited is a global, specialty biopharmaceutical company that researches, develops, manufactures and markets products to treat and prevent serious human medical conditions

Alexion is focused on developing and delivering life-transforming therapies for patients with devastating and rare diseases.

Diseasemaps - World Maps of Chronic and Rare Diseases and other Syndromes and Conditions. Connect with people who share your condition and help each other.

Gamuts: Comprehensive radiology differential diagnosis. Linking imaging findings to diseases and clinical images.

Biogen develops, manufactures and markets innovative therapies for patients living with serious neurological, autoimmune and rare diseases.

StudyPages is a self-service study listing platform to quickly set up a dedicated webpage for a research study, share with target communities using social media, and track signups. StudyPages by Yuzu Labs was created to bring human research online, accelerate it, and make it part of everyone's daily life.

Perlara PBC is a scientific discovery company finding treatments for rare diseases previously believed to be too rare to cure.

Sequencing 100,000 DNA codes of patients, leading to better, earlier diagnosis and personalised care, for cancer, rare diseases and infectious diseases.

Combined we are the leading global biotechnology company focused on serving patients with rare diseases and specialty conditions. Learn more about how we're shaping what's next.

EURORDIS - Rare Diseases Europe, is a non-governmental patient-driven alliance of rare disease patient organisations representing 745 rare diseases patient organisations in 65 countries. We are dedicated to improving the quality of life of all people living with rare diseases in Europe

CSL Limited is a global, specialty biopharmaceutical company that researches, develops, manufactures and markets products to treat and prevent serious human medical conditions

Our commitment to transforming the lives of people with rare diseases drives what we do.

Ultra rare disease foundation is here to help you find more information about Ultra rare diseases as well as help you connect with families experiencing a similar life

AveXis is focused on developing gene therapy for patients with rare and life-threatening neurological genetic diseases, like spinal muscular atrophy (SMA).

JP2MRI is a non-profit medical research institute devoted to find cures for medical diseases for the use of ethical adult stem cells.

Conferenceseries.com organizing Infectious Diseases Conferences in USA, Europe, Australia and other prominent locations across the globe. We organise Infectious diseases meetings in the fields related to Infectious diseases like Bacteriology, parasitology and STD.

AGTC is developing cures for rare lung and eye diseases, offering hope to patients with unmet medical needs.

Amryt Pharma plc is a specialty pharmaceutical company focused on developing and delivering innovative new treatments for patients with rare and orphan diseases.

Dr. John G. McHenry is committed to the treatment, prevention and rehabilitation of neurologically related eye diseases and vision disorders. He is a leading Interventional Neuro-ophthalmologist who has trained the next generation of eye doctors in Oculoplastics, Orbital Surgery and the medical and surgical care of double vision. Dr. McHenry is the only interventional neuro-ophthalmologist in North Texas. He sees patient from all over North, East and West Texas as well as the Hill country, the Valley, the Panhandle, New Mexico, Oklahoma, Arkansas, Kansas, Missouri, Louisiana and Mississippi and consults on rare and complicated eye conditions across the country.

Sapientia developed by leading scientists and clinicians facilitates diagnosis of rare genetic diseases. Easy to use tailored genome interpretation reports.

HORAMA develops innovative gene therapy products for rare ophthalmic diseases to preserve visual autonomy in affected patients.

SERB is a European specialty pharmaceutical group focused on prescription medicines which address rare and life-threatening diseases.

The MacArthur lab uses cutting-edge genomic technologies at massive scale to understand the impact of human genetic variation, and to provide answers to families affected by rare genetic diseases. exome aggregation We lead an international consortium that has assembled ExAC, the world's largest single collection of sequencing data from human protein-coding gene regions (the exome),…

more than 500 up to date discus photos Besides our discus hatchery, we have a full line aquarium fish store, specializing in discus and other rare community fish

Kaposi sarcoma is rare cancer type that affects the skin, lymph nodes and mouth. It was Moritz Kaposi who invented this cancer in 1872 and hence the name Kaposi

Symptom checker allowing research of the causes of one or many symptoms in an extensive knowledge base, including common and rare causes.

We specialise in strategic pricing and market access for rare and severe diseases

Actelion Pharmaceuticals UK Ltd is the UK affiliate of Actelion Pharmaceuticals Ltd, a biopharmaceutical company. Actelion focuses on the discovery, development and commercialization of innovative treatments to serve high unmet medical needs.

FutureNeuro is an SFI Research Centre to develop new technologies and solutions for the treatment, diagnosis, and monitoring of chronic and rare neurological diseases.

Biogen is one of the world’s leading biotechnology companies, with a focus on developing therapies for serious neurological, autoimmune and rare diseases.

Gamida Cell is committed to changing the treatment paradigm for patients with cancer and rare genetic diseases....

international, quarterly, peer reviewed journal that keeps cardiologists up to date with rare disorders of heart and vessels.

Rare diseases Sweden

Visit the virtualmedstudent.com for information on all aspects of health. Tutorials on both common and rare condition in easy to understand language. In addition, visit our video page for videos about common health issues.

Strongbridge.  Driven by passion. Focused on results. See how we’re bridging treatment gaps in rare diseases.